Home | Rare Diseases Clinical Research Network
WEBWho We Are. The RDCRN program is designed to advance medical research on rare diseases by providing support for clinical studies and facilitating collaboration, study enrollment and data sharing.
Clinical Trials - National Organization for Rare Disorders
WEBList of Rare Diseases; Gene Therapy for Rare Disease; Find Clinical Trials & Research Studies; For researchers. Request for Proposals; Research Grant Programs; Data Standards for Rare Diseases; For clinicians. Resources for Patients; Find a Rare Disease Care Center; Continuing Medical Education (CME) Connect. IAMRARE ® Program …
Clinical Trials — Rare Disease Research
WEBWe’re looking for volunteers to participate in clinical studies for a number of rare conditions. Contact us to learn more. If you might be a good fit for a clinical study, our team will reach out to you as soon as possible.
Rare-disease researchers pioneer a unique approach to clinical trials ...
WEBMay 5, 2023 · Rare-disease researchers pioneer a unique approach to clinical trials. Mike May. Nature Medicine 29 , 1884–1886 ( 2023) Cite this article. 14k Accesses. 3 Citations. 65 Altmetric....
Rare Diseases Clinical Research Network | National Center for …
WEBFebruary 29, 2024 - NCATS News. Our Impact on Rare Diseases. Rare Diseases Clinical Research Network (RDCRN) NEPTUNE’s research has helped us learn more about the biology of both rare and common kidney diseases. It has also led to better ways to diagnose and treat these conditions. Read Article.
Rare Research Report: February 2024 | Rare Diseases Clinical Research ...
WEBFeb 23, 2024 · A list of current and planned clinical trials for PKU gene therapy is also included. Authors note that this review can help advance scientific understanding and efficacy testing, paving the way for safe and efficient therapies for patients with PKU.
Designing clinical trials for rare diseases: unique challenges and ...
WEBMar 10, 2022 · Nevertheless, clinical trials for rare diseases can present inherent challenges. Optimal study design and partnerships between academia and industry are therefore required for the...
Information on Clinical Trials & Research Studies | NORD
WEBMore Than 95% of Rare Diseases Have No Treatment. Clinical Trials Are Essential for Identifying Therapeutic Options. Participating in a clinical trial can help you access investigational therapies intended to provide new or better ways to treat medical conditions.
Rare Research Report: December 2022 | Rare Diseases Clinical Research ...
WEBDec 5, 2022 · Rare Research Report: December 2022 | Rare Diseases Clinical Research Network. December 5, 2022. Each month, we share summaries of recent Rare Diseases Clinical Research Network (RDCRN) grant-funded publications. Catch up on the latest RDCRN research below. Jump to: Brittle Bone Disorders Consortium (BBDC)
Our Network | Rare Diseases Clinical Research Network
WEBWe are the Rare Diseases Clinical Research Network (RDCRN), an initiative of the Division of Rare Diseases Research Innovation (DRDRI) within the National Institutes of Health's National Center for Advancing Translational Sciences (NCATS). We are funded by NCATS and collaborating institutes and centers.
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